A baby diagnosed with a rare genetic disorder has shown remarkable improvement after receiving an experimental gene editing treatment tailored just for him. This groundbreaking therapy offers hope for others with similar conditions.
KJ Muldoon, born with a deadly genetic disorder, received a groundbreaking CRISPR treatment just six months after birth. His remarkable progress showcases the future of personalized medicine for rare diseases.
The final autopsy results of Gene Hackman and his wife, Betsy Arakawa, reveal shocking health conditions and the tragic circumstances surrounding their deaths, including hantavirus and advanced Alzheimer's.
Emily Kramer-Golinkoff, a cystic fibrosis patient with a rare mutation, highlights the struggles of those left behind as gene therapies show promise for others. Her journey underscores the need for equitable treatments in rare genetic conditions.
The world mourns the loss of Prince Frederik of Luxembourg, who passed away at just 22 due to a rare genetic condition. His father, Prince Robert, shares a heartfelt tribute highlighting Frederik's inspiring legacy and dedication to finding a cure.
