In a groundbreaking case, a 6-month-old baby boy named KJ was treated with a personalized CRISPR gene-editing therapy, correcting a dangerous mutation before it could threaten his life. This innovative approach promises hope for similar cases.
KJ Muldoon, born with a deadly genetic disorder, received a groundbreaking CRISPR treatment just six months after birth. His remarkable progress showcases the future of personalized medicine for rare diseases.